Chapter 3 AAV-vectored base editor transsplicing delivers dystrophin repair Zhen Li1 and Manuel A.F.V. Gonçalves1 Cell & Gene Therapy Insights 9:1201-1210 (2023) 1Leiden University Medical Centre, Department of Cell and Chemical Biology, Einthovenweg 20, 2333 ZC, Leiden, The Netherlands.
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