Chapter 6 —— 158 —— References 1. Pacesa M, Pelea O, Jinek M. Past, present, and future of CRISPR genome editing technologies. Cell 2024 187:1076-1100. 2. Doudna JA, Charpentier E. Genome editing. The new frontier of genome engineering with CRISPR-Cas9. Science 2014 346:1258096. 3. Koonin EV, Makarova KS, Zhang F. Diversity, classification and evolution of CRISPRCas systems. Curr Opin Microbiol. 2017 37:67-78. 4. Chen X, Gonçalves MAFV. DNA, RNA, and Protein Tools for Editing the Genetic Information in Human Cells. iScience 2018 6:247-263. 5. Chen X, Rinsma M, Janssen JM, Liu J, Maggio I, Gonçalves MA. Probing the impact of chromatin conformation on genome editing tools. Nucleic Acids Res. 2016 44:6482-92. 6. Liao H, Wu J, VanDusen NJ, Li Y, Zheng Y. CRISPR-Cas9-mediated homologydirected repair for precise gene editing. Mol Ther Nucleic Acids. 2024 35:102344. 7. Chen X, Janssen JM, Liu J, Maggio I, 't Jong AEJ, Mikkers HMM, Gonçalves MAFV. In trans paired nicking triggers seamless genome editing without double-stranded DNA cutting. Nat Commun. 2017 8:657. 8. Nakajima K, Zhou Y, Tomita A, Hirade Y, Gurumurthy CB, Nakada S. Precise and efficient nucleotide substitution near genomic nick via noncanonical homology-directed repair. Genome Res. 2018 28:223-230. 9. Wang Q, Liu J, Janssen JM, Gonçalves MAFV. Precise homology-directed installation of large genomic edits in human cells with cleaving and nicking high-specificity Cas9 variants. Nucleic Acids Res. 2023 51:3465-3484. 10. Chai AC, Chemello F, Li H, Nishiyama T, Chen K, Zhang Y, Sánchez-Ortiz E, Alomar A, Xu L, Liu N, Bassel-Duby R, Olson EN. Single-swap editing for the correction of common Duchenne muscular dystrophy mutations. Mol Ther Nucleic Acids. 2023 32:522-535. 11. Hanlon KS, Kleinstiver BP, Garcia SP, Zaborowski MP, Volak A, Spirig SE, Muller A, Sousa AA, Tsai SQ, Bengtsson NE, Lööv C, Ingelsson M, Chamberlain JS, Corey DP, Aryee MJ, Joung JK, Breakefield XO, Maguire CA, György B. High levels of AAV vector integration into CRISPR-induced DNA breaks. Nat Commun. 2019 10:4439. 12. Nelson CE, Wu Y, Gemberling MP, Oliver ML, Waller MA, Bohning JD, RobinsonHamm JN, Bulaklak K, Castellanos Rivera RM, Collier JH, Asokan A, Gersbach CA. Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy. Nat Med. 2019 25:427-432. 13. Chen X, Gonçalves MA. Engineered Viruses as Genome Editing Devices. Mol Ther. 2016 24:447-457.
RkJQdWJsaXNoZXIy MTk4NDMw