Chapter 5 —— 139 —— Supplementary Information >BI17_pAAV-HRS1.A1 (4304 bp) ctggcgcgctcgctcgctcactgaggccgcccgggcaaagcccgggcgtcgggcgacctttggtcgcccggcct cagtgagcgagcgagcgcgcagagagggagtggccaactccatcactaggggttccttgtagttaatgattaac ccgccatgctacttatctacgtggccactagtacttctcgagctctgtacatgtccgcggtcgcgacgtacgcg tatcgatggcgccagctgcagagctctagctcttccagccccctgtcatggcatcttccaggggtccgagagct cagctagtcttcttcctccaacccgggcccctatgtccacttcaggacagcatgtttgctgcctccagggatcc tgtgtccccgagctgggaccaccttatattcccagggccggttaatgtggctctggttctgggtacttttatct gtcccctccaccccacagtggggcaagcttccacggggttggggttgcgccttttccaaggcagccctgggttt gcgcagggacgcggctgctctgggcgtggttccgggaaacgcagcggcgccgaccctgggtctcgcacattctt cacgtccgttcgcagcgtcacccggatcttcgccgctacccttgtgggccccccggcgacgcttcctgctccgc ccctaagtcgggaaggttccttgcggttcgcggcgtgccggacgtgacaaacggaagccgcacgtctcactagt accctcgcagacggacagcgccagggagcaatggcagcgcgccgaccgcgatgggctgtggccaatagcggctg ctcagcagggcgcgccgagagcagcggccgggaaggggcggtgcgggaggcggggtgtggggcggtagtgtggg ccctgttcctgcccgcgcggtgttccgcattctgcaagcctccggagcgcacgtcggcagtcggctccctcgtt gaccgaatcaccgacctctctccccaccggtcgccaccatggtgagcaagggcgaggagctgttcaccggggtg gtgcccatcctggtcgagctggacggcgacgtaaacggccacaagttcagcgtgtccggcgagggcgagggcga tgccacctacggcaagctgaccctgaagttcatctgcaccaccggcaagctgcccgtgccctggcccaccctcg tgaccaccctgacctacggcgtgcagtgcttcagccgctaccccgaccacatgaagcagcacgacttcttcaag tccgccatgcccgaaggctacgtccaggagcgcaccatcttcttcaaggacgacggcaactacaagacccgcgc cgaggtgaagttcgagggcgacaccctggtgaaccgcatcgagctgaagggcatcgacttcaaggaggacggca acatcctggggcacaagctggagtacaactacaacagccacaacgtctatatcatggccgacaagcagaagaac ggcatcaaggtgaacttcaagatccgccacaacatcgaggacggcagcgtgcagctcgccgaccactaccagca gaacacccccatcggcgacggccccgtgctgctgcccgacaaccactacctgagcacccagtccgccctgagca aagaccccaacgagaagcgcgatcacatggtcctgctggagttcgtgaccgccgccgggatcactctcggcatg gacgagctgtacaagtaaagcggccggccgcgtcgagtctaggatcagcctcgactgtgccttctagttgccag ccatctgttgtttgcccctcccccgtgccttccttgaccctggaaggtgccactcccactgtcctttcctaata aaatgaggaaattgcatcgcattgtctgagtaggtgtcattctattctggggggtggggtggggcaggacagca agggggaggattgggaagacaatagcaggcatgctggggatgcggtgggctctatggaagctttactagggaca ggattggtgacagaaaagccccatccttaggcctcctccttcctagtctcctgatattgggtctaacccccacc tcctgttaggcagattccttatctggtgacacacccccatttcctggagccatctctctccttgccagaacctc taaggtttgcttacgatggagccagagaggatcctgggagggagagcttggcagggggtgggagggagctagag tccggccgcccccttcaccgagggcctatttcccatgattccttcatatttgcatatacgatacaaggctgtta gagagataattggaattaatttgactgtaaacacaaagatattagtacaaaatacgtgacgtagaaagtaataa tttcttgggtagtttgcagttttaaaattatgttttaaaatggactatcatatgcttaccgtaacttgaaagta tttcgatttcttggctttatatatcttgtggaaaggacgaaacaccggggccactagggacaggatgtttcaga gctatgctggaaacagcatagcaagttgaaataaggctagtccgttatcaacttgaaaaagtggcaccgagtcg gtgctttttttgaattcactggccgtcgttttacaacgtcgtgactgggaaaaccctggcgttacccaacttaa tcgccttgcagcacatccccctttcgccagaacaaccggtaccaaatttattgatggatcaatttaaagagttt taatctgggtgttatgagttccttgggcctattgtttgcctgaaccctgtggggactggctcatcagcagaatt attcatggaggaatttgctaggttttaccttggctctctagcttgggacattttgtttcttccttaaatcctta ttgcaaccgtccagctaccaggtaggtatattgccttgtaagtgctggtacagtttgccttatttatattccac tgcttctcagggattaacatctgctcgtgcagctgagatcctggcgcgagatggtcccaacgccctcactcccc ctcccactactcctgaatggatcaagttttgtcggcagctctttggggggttctcaatgttactgtggattgga gcgattctttgtttcttggcttatagcatcagagctgctacagaagaggaacctcaaaacgatgacgtgagttc
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